Center for Orphan Disease Research & Therapy

Outside Funding Opportunities

Request for Proposals: National Organization for Rare Disorders Research Grant Program

  • Cystic Fibrosis Foundation LeRoy Matthews Physician/Scientist Award
    Closes 09/10/2014 Inquire with Funder
  • Cystic Fibrosis Foundation Harry Shwachman Clinical Investigator Award
    Closes 09/10/2014 Inquire with Funder
  • Desmoid Tumor Research Foundation
    Closes 09/15/2014 Inquire with Funder
  • 2014 Angelman Syndrome Foundation Joseph E. Wagstaff Postdoctoral Fellowship Grant
    Closes:10/01/2014 Maximum:$110,000
  • Prader-Willi Syndrome Association Research Grant Program
    Closes:10/07/2014 Maximum:$75,000
  • Progeria Research Foundation Research Grant Program
    Closes:10/27/2014 Maximum: Inquire with Funder
  • Sjogren's Syndrome Foundation Research Grants Program
    Closes:02/01/2015 Maximum:$100,000
  • FRAXA Research Foundation Grants and Fellowships Program
    Closes:02/01/2015 Maximum:$100,000
  • Shwachman-Diamond Syndrome Foundation Research Grant Program
    Closes:03/12/2015 Maximum:$70,000
  • Cornelia de Lange Syndrome Foundation Research Grant Program
    Closes:04/30/2015 Maximum:$20,000

Links to Outside Resources

Other Research Opportunities:

Lymphatic Malformation Institute (LMI) ) was established in December, 2010, and is focused, as a whole, on advancing the understanding of the lymphatic system and, specifically, advancing the understanding of the rare lymphatic malformations, Lymphangiomatosis and Gorham's Disease.

The goal of the LMI is to find cures and treatments for these life-threatening disorders that have received very little attention from the scientific community in the past. The LMI seeks to fill this critical gap by identifying, organizing and funding research studies by medical and research professionals, and also working closely with other foundations with similar objectives.  Click here for more information.

The Foundation for Prader-Willi Research (FPWR), a nonprofit organization dedicated to supporting research to advance the understanding and treatment of Prader-Willi syndrome (PWS), announces the availability of funds to support innovative research relevant to PWS. FPWR is particularly interested in supporting projects that will lead to new interventions to alleviate the symptoms associated with PWS.

Priority will be given to the following areas of research, although alternative areas of high scientific merit will also be considered:

  • Molecular basis of the PWS phenotype
  • Regulation of appetite and energy homeostasis in individuals with PWS; development and evaluation of therapeutic interventions to regulate appetite and satiety in PWS
  • Etiology of medical, behavioral and psychiatric complications in PWS; development and evaluation of therapeutic interventions
  • Development of novel therapeutic interventions using in vitro and in vivo models of PWS

A more complete list of research priorities may be found here.

Funds Available: Applicants may request up to $100,000 USD in direct costs for the initial year of support, with the possibility of a second year of funding upon competitive renewal.  Indirect costs of up to 8% are allowed. Letter of Intent Due Date:  September 8th, 2014 5pm EST.

For more information: 

Outside Events of Interest:

National Organization for Rare Diseases 2014 Annual Conference, October 21-22, Alexandria, VA
Conference web-site:

Website information RE: Scientific Poster Session. .

The deadline for submission for poster abstracts was July 18, 2014.