Orphan Disease Center

Rare Disease Overview ODC Opportunities

RFA-Improved Therapies for Rare Diseases - MDBR Pilot Grants and Postdoctoral Fellowships

As a result of the Million Dollar Bike Ride, the Orphan Disease Center announces a Request for Applications (RFA) to support research from fundraising efforts for $50,000–$65,000 Pilot Grants, and $35,000 Postdoctoral Fellowship Grants.  International applications are welcome; the RFA is not restricted to Penn/CHOP or USA researchers.

Pilot grants are available for research related to:

Adrenoleukodystrophy (ALD), Congenital Hyperinsulinism (CHI), Lymphangioleiomyomatosis (LAM), Mucolipidosis Type IV, Niemann Pick Type C (NPC), Pitt Hopkins,and RASopathies

Postdoctoral Fellowships are available for research related to:

Congenital Muscular Dystrophy (CMD), Homozygous Familial Hypercholesterolemia (HoFH), Friedreich's Ataxia (FRDA),Hemophilia, Mucopolysaccharidosis (MPS), Niemann Pick Type C (NPC), and Tay-Sachs and related disorders

The timeline for the RFA/grant program is as follows:

  • RFA Posted: August 1, 2014
  • Pre-application deadline: September 15, 2014, documents are to be uploaded no later than 5pm - PRE-APPLICATION IS CLOSED!
  • Invitation to submit a Full-application by September 23, 2014
  • Full-application deadline: October 20, 2014 (by invitation only) documents are to be uploaded no later than 8PM EST
  • Anticipated start date: December 1, 2014

Full Application Information:

All applicants must become a member in the Orphan Disease Center to participate in this RFA. Please view our membership details.