Cideciyan Lab

• News

News mentioning our research

• October 2018
  • Ophthotec: Ophthotech Expands Gene Therapy Pipeline in Orphan Retinal Diseases with Exclusive Option for Novel Product Candidates to Treat Best Vitelliform Macular Dystrophy (Best Disease)
• August 2018
  • Penn News: Knockdown and replace: A gene therapy twofer to treat blindness
  • NIH NEI: Researchers find potential new gene therapy for blinding disease: Scientists funded by NIH preserve vision in dogs with a disease similar to retinitis pigmentosa in humans
  • Philadelphia Inquirer: Penn’s experimental gene therapy saves night vision in dogs, paving the way for human tests
  • UPI: New gene therapy treats inherited eye disorders in animal study
  • Ophthotec: Scientific Data for Novel Adeno-Associated Virus Gene Therapy in Rhodopsin-Mediated Autosomal Dominant Retinitis Pigmentosa Published in Proceedings of the National Academy of Sciences
• June 2018
  • Ophthotec: Ophthotech Enters into Gene Therapy Agreements with the University of Florida and the University of Pennsylvania
• April 2018
  • FFB: Groundbreaking Research for Inherited Retinal Diseases Funded by Foundation Fighting Blindness to be Showcased at ARVO
• March 2018
  • Penn News: New Gene Therapy Corrects a Form of Inherited Macular Degeneration in Canine Model
  • GEN: Gene-Therapy Trials for Inherited Form of Blindness Could Start in Two Years
  • Technology Networks: Best Disease Blindness Bettered By Gene Therapy
  • BPoD: Blind Spot
  • FFB: Best Disease Gene Therapy Advances Toward Clinical Trial
• December 2017
  • ARVO: 2018 Achievement Award Recipients
• November 2017
  • ProQR: ProQR Doses First LCA 10 Patient in Clinical Trial of QR-110, ProQR’s Lead Program for Genetic Blindness
• August 2017
  • AGTC: Research Published in Molecular Therapy Identifies Optimal Gene-based Therapeutic Construct for X-Linked Retinitis Pigmentosa
• August 2016
  • Penn News: Penn: Blinding Disease in Canines and Humans Shares Causative Gene, Pathology
• December 2015
  • BPoD: Battling Blindness
• October 2015
  • NEI News: Gene Therapy Staves Off Blindness from Retinitis Pigmentosa in Canine Model
  • Penn News: Penn Study Stops Vision Loss in Late-stage Canine X-linked Retinitis Pigmentosa
  • Scicasts: Study Stops Vision Loss in Late-stage Canine X-linked Retinitis Pigmentosa
  • FFB News: XLRP Gene Therapy Rescues Vision in Late-Stage Disease 
• May 2015
  • NEI News: Benefits for Leber Congenital Amaurosis Peak after One to Three Years, then Diminish
  • Penn News: Penn Study Indicates that Gene Therapy Efficacy for LCA is Dynamic: Improvement is Followed by Decline in Vision
  • Science Now: Gene Therapy for Blindness May Fade with Time
• Sept 2014
  • Nature News: Curing blindness: Vision quest
• March 2014
  • Penn News: Anatomical Discovery by Penn Team Gives Insight into Blinding Retinal Diseases
• January 2013
  • NEI News: New Findings Suggest Need for Combined Strategy in Treatment of Rare Form of Blindness
  • Penn News: Penn Study Sheds Light on the Complexity of Gene Therapy for Congenital Blindness
• January 2012
  • Penn News: Gene Therapy Research Team From Penn Vet and Scheie Eye Institute Cures Retinitis Pigmentosa in Dogs 
  • NEI News: Canine Study Puts Gene Therapy for X-linked Retinitis Pigmentosa in Sight
• August 2011
  • EurekAlert: Scientists Unravel the Cause of Rare Genetic Disease: Goldman-Favre Syndrome Explained
• August 2009
  • EurekAlert: Vision Improvement after Gene Therapy Maintained at 1 Year for Inherited Retinal Blindness
  • MIT Technology Review: Gene Therapy Creates a New Fovea
  • EurekAlert: Vision Researchers See Unexpected Gain a Year into Blindness Trial
• September 2008
  • NEI News: Promising Results in Phase 1 Gene Therapy Trial for Blinding Disease
  • EurekAlert: Safety Study Indicates Gene Therapy for Blindness Improves Vision
• November 2007
  • EurekAlert: Gene Therapy Safety Trial for Childhood Blindness Under Way
• June 2007
  • EurekAlert: Penn Researchers Report that Gene Therapy Awakens the Brain Despite Blindness from Birth
• May 2006
  • EurekAlert: Gene Therapy for Chicken Model of Childhood Blindness