Clinical Trials
There are several clinical trials that are currently ongoing:
Indication |
Phase |
Treatment |
More information at ClinicalTrials.gov |
LCA1 / GUCY2D |
1/2 |
Subretinal gene augmentation |
|
LCA5 / Lebercilin |
1/2 |
Subretinal gene augmentation |
|
LCA10 / CEP290 |
1/2 |
Subretinal gene editing |
|
RP |
3 |
Oral N-acetylcysteine |
|
XLRS | 1/2 | Subretinal gene augmentation | NCT05878860 |