Clinical Trials
There are several clinical trials that are currently ongoing at CHRD:
|
Indication |
Phase |
Treatment |
More information at ClinicalTrials.gov |
|
LCA1 / GUCY2D |
1/2 |
Subretinal gene augmentation |
|
|
LCA5 / Lebercilin |
1/2 |
Subretinal gene augmentation |
|
|
LCA10 / CEP290 |
1/2 |
Subretinal gene editing |
|
|
RP |
3 |
Oral N-acetylcysteine |
|
| XLRS | 1/2 | Subretinal gene augmentation | NCT05878860 |
| RPGR-XLRP | 2/3 | Subretinal gene augmentation | |
| USH2A | 2 | Intravitreal antisense oligonucleotide | NCT06627179 |
| LCA10 / CEP290 | 3 | Intravitreal antisense oligonucleotide | NCT06891443 |