Clinical Trials
There are several clinical trials that are currently active at CHRD:
|
Indication |
Recruiting |
Phase |
Treatment |
More information at ClinicalTrials.gov |
|
LCA1 / GUCY2D |
Y |
1/2/3 |
Subretinal gene augmentation |
|
|
LCA5 / Lebercilin |
Y |
1/2/3 |
Subretinal gene augmentation |
|
|
LCA10 / CEP290 |
Y |
3 |
Intravitreal antisense oligonucleotide |
|
|
XLRS |
Y |
1/2 |
Subretinal gene augmentation |
|
|
ABCA4 |
Y |
1/2 |
Subretinal RNA exon editing |
|
|
LCA10 / CEP290 |
N |
1/2 |
Subretinal gene editing |
|
|
RP |
N |
3 |
Oral N-acetylcysteine |
|
|
RPGR-XLRP |
N |
2/3 |
Subretinal gene augmentation |
|
|
USH2A |
N |
2 |
Intravitreal antisense oligonucleotide |