Platelet-Targeted Gene Therapy for Hemophilia A with Inhibitor History.

Eapen M, Malec LM, Armant MA, Johnson BD, Shi Q, Xu H, Du LM, Jerkins JH, Duffy LJ, Bushman FD, Lee C, Petrichenko A, Hematti P, Brazauskas R, Jobe SM, Hari PN, Wilcox DA. N Engl J Med. 2025 Jan 23;392(4):412-414. doi: 10.1056/NEJMc2415164. PMID: 39842018