Publications
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Validation of high-sensitivity assays to quantitate cerebrospinal fluid and serum β-galactosidase activity in patients with GM1-gangliosidosis
Karen J. Quadrini, Catherine Vrentas, Christian Duke, Chris Wilson, Christian J. Hinderer, David A. Weinstein, Samiah A. Al-Zaidy, Susan E. Browne, James M. Wilson, Yan G. Ni
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Lipid Nanoparticle mRNA Therapy Improves Survival and Reduces Serum Branched-Chain Amino Acids in Mouse Models of Maple Syrup Urine Disease
Jenny A Greig, Matthew Jennis, Aditya Dandekar, Joanna K Chorazeczewski, Nesteene Param, Meardey So, Mohamad Nayal, Peter Bell, Kimberly Coughlan, Minjung Choi, Paloma H Giangrande, Paolo G V Martini, James M Wilson
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Modulation of AAV9 Galactose Binding Yields Novel Gene Therapy Vectors and Predicts Cross-Species Differences in Glycan Avidity
Jacob A Hoffman, Nathan Denton, Joshua J Sims, Rosemary Meggersee, Zhe Zhang, Kanyin Olagbegi, James M Wilson