Amy Tara Waldman, M.D., M.S.C.E.
Associate Professor of Neurology at the Children's Hospital of Philadelphia
Medical Director, Leukodystrophy Center of Excellence, Children's Hospital of Philadelphia
Associate Director of Neurology Gene Therapy, Children's Hospital of Philadelphia
Department: Neurology
Contact information
Children's Hospital of Philadelphia
Division of Neurology
3401 Civic Center Boulevard
Philadelphia, PA 19104
Division of Neurology
3401 Civic Center Boulevard
Philadelphia, PA 19104
Office: 215-590-1719
Fax: 215-590-1771
Fax: 215-590-1771
Email:
waldman@chop.edu
waldman@chop.edu
Education:
B.A. (Chemistry)
Johns Hopkins University, 1997.
M.D. (Medicine)
Jefferson Medical College, 2002.
M.S.C.E. (Epidemiology)
Perelman School of Medicine at the University of Pennsylvania, 2011.
Permanent linkB.A. (Chemistry)
Johns Hopkins University, 1997.
M.D. (Medicine)
Jefferson Medical College, 2002.
M.S.C.E. (Epidemiology)
Perelman School of Medicine at the University of Pennsylvania, 2011.
Selected Publications
Keselman DJ, Small JC, Seneviratne T, McCague S, Kaschak TL, Yum SW, O'Brien A, Brandsema JF, Diamond T, Loomes KM, Lin KY, Wittlieb-Weber CA, Mayer OH, Daniel SG, Waldman AT, Samelson-Jones BJ, Matesanz SE, George LA: Real-world outcomes of delandistrogene moxeparvovec gene therapy: Motor outcomes and emerging safety concerns. Mol Ther 7(34(1)): 123-130, Jan 2026.Levin D, Levin J, Joung J, Liu GW, Donaher J, Faig W, Waldman AT: Language Skills in Patients With Alexander Disease. Am J Speech Lang Pathol 13(35(1)): 211-225, Jan 2026.
Waldman AT, Takanohashi A, Joung JY, Liu GW, Arnold K, Pizzino A, Faig W, Woidill S, Narula S, Vanderver AL: Characterization of Clinical Phenotype to Glial Fibrillary Acidic Protein Concentrations in Alexander Disease. Ann Clin Transl Neurol Jan 2026 Notes: Epub ahead of print.
Caplash S, Song H, Waldman A, Ying GS, Kim BJ: Characteristics of Study Design and Statistical Analysis in Optical Coherence Tomography Based Studies of Neurodegeneration. Ophthalmology Science October 2025 Notes: In press.
Keselman DJ, Small JC, Seneviratne T, McCague S, Kaschak TL, Yum SW, O’Brien A, Brandsema JF, Diamond T, Loomes KM, Lin KY, Wittlieb-Weber CA, Mayer OH, Daniel SG, Waldman AT, Samelson-Jones BJ, Matesanz SE, George LA: Real-World Outcomes of Delandistrogene Moxeparvovec Gene Therapy: Motor Outcomes and Emerging Safety Concerns. Molecular Therapy Epub ahead of print, October 2025.
Kotes ER, Woidill S, D'Aiello R, Khan A, McCann J, Ramos M, Gavazzi F, Keller S, Van Haren K, Fatemi A, Eichler F, Bonkowsky J, Fraser J, Emrick L, Sherbini O, Hackett A, Gauna J, Amos D, Goodman J, Fine AS, Nagy A, Lee S, Page N, Schmidt J, Pizzino A, Muirhead K, Bennett M, Waldman A, Shults J, Adang L, Grundmeier R, Vanderver A.: Clinically Important Endpoints in Individuals With Leukodystrophy: A Multisite Study. Ann Child Neurol Soc July 2025.
Goyne C, Fair AE, Yilmaz D, Race J, Schuette A, Caillier SJ, Aaen GS, Abrams AW, Benson LA, Casper TC, Chitnis T, Gorman MP, Lotze TE, Krupp LB, Mar SS, Ness JM, Rensel M, Rodriguez M, Rose JW, Schreiner TL, Tillema JM, Waldman AT, Wheeler YS, Barcellos LF, Waubant E, Graves JS; as the US Network of Pediatric MS Centers: Epigenetic Aging in Pediatric-Onset Multiple Sclerosis. Neurology 104(12): e213673, Jun 2025.
Messing A, Waldman AT, Bolt DM: Genotype-Phenotype Association for 14 GFAP Variants in Alexander Disease. Neurology Genetics 11(3): e200270, Jun 2025.
Lynch DS, Wade C, Carlson AK, Barkhof F, Yoshida T, Collins A, Edwards MR, Waldman AT: Diagnosing Alexander disease in adults. Pract Neurol May 2025 Notes: Online ahead of print.
Joung JY, Gallison KJ, Liu GW, Berger JA, Drum ET, Dubow SR, McClung HA, Faig W, Avery RA, Liu GT, Narula S, Vossough A, Waldman AT: Prevalence of Elevated Opening Pressure Measurements in Alexander Disease. Pediatr Neurol 168: 105-111, May 2025.